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First new treatment in 30 years for rare disease is effective, tolerable, convenient
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/content/first-new-treatment-30-years-rare-disease-effective-tolerable-convenient
/neurologyreviews/article/266401/rare-diseases/first-new-treatment-30-years-rare-disease-effective
/neurology/article/266401/rare-diseases/first-new-treatment-30-years-rare-disease-effective-tolerable